Supported projects
Conception of chemical chaperones
Last Updated on Thursday, 04 March 2010 11:13
Conception and evaluation of new chemical chaperones of the N-acetyglucosaminidase in the context of the development of a treatment for Sanfilippo Syndrome (MPS III B).
Gene Therapy
Last Updated on Thursday, 04 March 2010 11:03
(program organized by Sanfilippo alliance)
As we have mentioned, one of the ongoing research projects is the intracerebral gene therapy program.
Bone marrow transplant
Last Updated on Thursday, 04 March 2010 11:10 Monday, 01 February 2010 12:55
Following our call for bids at the beginning of 2009 with the aim of endorsing (a) promising research program(s) for children with Mucopolysaccharidosis (MPS), the foundation selected Dr. Adeline Lau’s molecular genetic pathology project (Australia). Dr. Lau has worked for several years with this disorder.
